Gene therapy in mouse fetuses treats deadly disease

The method could minimize damage from disease if a condition is diagnosed in utero.

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Gene therapy administered in the womb could be used to treat a deadly genetic disease, a study in fetal mice suggests. The results could add to the increasingly popular notion of prenatal gene therapy as a way to minimize the damage wrought by some genetic diseases. The US Food and Drug Administration approved the first gene therapy for adults and children last year, and more treatments are crowding pharmaceutical pipelines around the world.

By Heidi Ledford, Nature News


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